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Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851

Genome Medical Sequencing for Gene Discovery

Namoota walitti qabaa jiraQorannoo ilaalaa
4 Weeks – 99 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT01087320

Screening Protocol for Genetic Diseases of Lymphocyte Homeostasis and Programmed Cell Death

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1 Month – 100 Years · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT00246857

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 2 hanga 17 · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT07441876

Familial Mediterranean Fever and Related Disorders: Genetics and Disease Characteristics

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
2 Months – 115 Years · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00001373

Evaluation of Patients With Immune Function Abnormalities

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00128973

Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granulocytes

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00001405

A Long-Term Observational Study of Patients With Fucosidosis

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

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7 Months – 15 Months · Saalaa hunda · Haaromfame 31-Hag-2026 · NCT06805695

Investigating Hereditary Risk In Thoracic Cancers (INHERIT)

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 26-Hag-2026 · NCT05587439

Studying Childhood-onset Behavioral, Psychiatric, and Developmental Disorders

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
30 Days – 99 Years · Saalaa hunda · Haaromfame 24-Hag-2026 · NCT01778504

Acceptance and Commitment Therapy for Caregivers of Children With a RASopathy: An Internal Pilot Feasibility Study and Follow-up Randomized Controlled Trial

Namoota walitti qabaa jiraHojjettoota fayyaa simatamoo
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 24-Hag-2026 · NCT05361811

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 05-Hag-2026 · NCT07224360

Inherited Reproductive Disorders

Namoota walitti qabaa jiraQorannoo ilaalaa
6 Weeks – 120 Years · Saalaa hunda · Haaromfame 28-Ado-2026 · NCT01500447

Prospective Clinical Assessment Study in Children With Hypochondroplasia

Namoota walitti qabaa jiraQorannoo ilaalaa
30 Months – 16 Years · Saalaa hunda · Haaromfame 16-Ado-2026 · NCT06410976

Genetic and Metabolic Disease in Children

Namoota walitti qabaa jiraQorannoo ilaalaa
1 Day · Saalaa hunda · Haaromfame 02-Ado-2026 · NCT02650622

Rett Syndrome Registry

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349

Rifampin in CYP24A1-related Hypercalcemia and Hypercalciuria

Namoota walitti qabaa jiraSadarkaa 2
6 Months – 65 Years · Saalaa hunda · Haaromfame 22-Wax-2026 · NCT03301038

ARPKD Database Study

Namoota walitti qabaa jiraQorannoo ilaalaa
Hanga umuriin 18 · Saalaa hunda · Haaromfame 15-Wax-2026 · NCT01401998

A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 12 fi ol · Saalaa hunda · Haaromfame 03-Wax-2026 · NCT07001280

UW Undiagnosed Genetic Diseases Program

Namoota walitti qabaa jiraQorannoo ilaalaa
Hanga umuriin 100 · Saalaa hunda · Haaromfame 29-Cam-2026 · NCT04586075

Genetic Disorders of Obesity Program Database

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 12-Cam-2026 · NCT05747976

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.