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Takkalaa qorannoo (Ingiliffa)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
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1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851Genome Medical Sequencing for Gene Discovery
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4 Weeks – 99 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT01087320Screening Protocol for Genetic Diseases of Lymphocyte Homeostasis and Programmed Cell Death
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1 Month – 100 Years · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT00246857Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
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Umuriin 2 hanga 17 · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT07441876Familial Mediterranean Fever and Related Disorders: Genetics and Disease Characteristics
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2 Months – 115 Years · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00001373Evaluation of Patients With Immune Function Abnormalities
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Umuriin hundi · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00128973Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granulocytes
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Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00001405A Long-Term Observational Study of Patients With Fucosidosis
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Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
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Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
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7 Months – 15 Months · Saalaa hunda · Haaromfame 31-Hag-2026 · NCT06805695Investigating Hereditary Risk In Thoracic Cancers (INHERIT)
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 26-Hag-2026 · NCT05587439Studying Childhood-onset Behavioral, Psychiatric, and Developmental Disorders
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30 Days – 99 Years · Saalaa hunda · Haaromfame 24-Hag-2026 · NCT01778504Acceptance and Commitment Therapy for Caregivers of Children With a RASopathy: An Internal Pilot Feasibility Study and Follow-up Randomized Controlled Trial
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 24-Hag-2026 · NCT05361811A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
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Umuriin 18 hanga 80 · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 05-Hag-2026 · NCT07224360Inherited Reproductive Disorders
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6 Weeks – 120 Years · Saalaa hunda · Haaromfame 28-Ado-2026 · NCT01500447Prospective Clinical Assessment Study in Children With Hypochondroplasia
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30 Months – 16 Years · Saalaa hunda · Haaromfame 16-Ado-2026 · NCT06410976Genetic and Metabolic Disease in Children
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1 Day · Saalaa hunda · Haaromfame 02-Ado-2026 · NCT02650622Rett Syndrome Registry
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349Rifampin in CYP24A1-related Hypercalcemia and Hypercalciuria
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6 Months – 65 Years · Saalaa hunda · Haaromfame 22-Wax-2026 · NCT03301038ARPKD Database Study
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Hanga umuriin 18 · Saalaa hunda · Haaromfame 15-Wax-2026 · NCT01401998A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 03-Wax-2026 · NCT07001280UW Undiagnosed Genetic Diseases Program
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Hanga umuriin 100 · Saalaa hunda · Haaromfame 29-Cam-2026 · NCT04586075Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
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Umuriin 4 hanga 18 · Dhiroota · Haaromfame 27-Cam-2026 · NCT07608432Genetic Disorders of Obesity Program Database
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Umuriin hundi · Saalaa hunda · Haaromfame 12-Cam-2026 · NCT05747976Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.