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A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Barrow Neurological Institute, Phoenix
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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Pompe Disease Registry Protocol

  • Barrow Neurological Institute- Site Number : 840087, Phoenix
  • Phoenix Children's Hospital- Site Number : 840003, Phoenix
  • University of Arizona- Site Number : 840015, Tucson
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • Barrow Neurol Group- Site Number : 840087, Phoenix
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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.