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A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
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Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155Pompe Disease Registry Protocol
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400Pompe Pregnancy Sub-Registry
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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
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Umuriin hundi · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT01665326Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 17-Bit-2026 · NCT07478172A Global Prospective Observational Registry of Patients With Pompe Disease
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Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011Cognitive and Neurological Pathologies in Pompe Disease
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Umuriin 0 hanga 18 · Saalaa hunda · Haaromfame 04-Bit-2026 · NCT04639336Avalglucosidase Alfa Pregnancy Study
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Umuriin hundi · Dubartoota · Haaromfame 16-Ama-2026 · NCT05734521Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.