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A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Disease Registry Protocol

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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease

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Umuriin hundi · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT01665326

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 17-Bit-2026 · NCT07478172

A Global Prospective Observational Registry of Patients With Pompe Disease

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Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Cognitive and Neurological Pathologies in Pompe Disease

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Umuriin 0 hanga 18 · Saalaa hunda · Haaromfame 04-Bit-2026 · NCT04639336

Avalglucosidase Alfa Pregnancy Study

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Umuriin hundi · Dubartoota · Haaromfame 16-Ama-2026 · NCT05734521

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.