Gara Jalqabaatti › Dhukkubaa Kuusaa Glycogen Gosa II › California
Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen Gosa II California keessatti
Qorannoo 5 Dhukkubaa Kuusaa Glycogen Gosa II f California keessatti hirmaatuu jiru.
Magaalota California keessatti
Takkalaa qorannoo (Ingiliffa)
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
- University of California-Irvine, Irvine
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- University of California, Irvine (UCI), Irvine
- Stanford Neuroscience Health Center, Palo Alto
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of California - Irvine Medical Center, Irvine
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155Pompe Disease Registry Protocol
- University of California at Irvine- Site Number : 840036, Irvine
- Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
- Children's Hospital of Orange County- Site Number : 840074, Orange
- fi 3 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400A Global Prospective Observational Registry of Patients With Pompe Disease
- University of California Irvine, Irvine
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.