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Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of Florida (UF) - Gainesville, Gainesville
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Disease Registry Protocol

  • University of Miami- Site Number : 840006, Coral Gables
  • University of Florida College of Medicine- Site Number : 840012, Gainesville
  • University of Florida Pediatrics Genetics- Site Number : 840121, Jacksonville
  • fi 1 dabalataa
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • University of Florida Pediatrics Genetics- Site Number : 157138, Jacksonville
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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Wolfson Children's Hospital, Jacksonville
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Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.