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Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen Gosa II Missouri keessatti

Qorannoo 6 Dhukkubaa Kuusaa Glycogen Gosa II f Missouri keessatti hirmaatuu jiru.

Magaalota Missouri keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Washington University School of Medicine, St Louis
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT07354724

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Washington University in St. Louis, St Louis
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Disease Registry Protocol

  • University of Missouri Health System Department of Genetics- Site Number : 840031, Columbia
  • Washington University- Site Number : 840100, St Louis
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • Washington University- Site Number : 150612, St Louis
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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

  • NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 17-Bit-2026 · NCT07478172

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Washington University School of Medicine, St Louis
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Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.