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Gara Jalqabaatti › Dhukkubaa Kuusaa Glycogen Gosa II › New York

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A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • NYU Langone, New York
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Pompe Disease Registry Protocol

  • NYU Langone Health - Perlmutter Cancer Center - Huntington- Site Number : 840040, Huntington
  • Northwell Health- Site Number : 840102, New Hyde Park
  • Icahn School of Medicine at Mount Sinai- Site Number : 840005, New York
  • fi 4 dabalataa
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • New York University School Of Medicine- Site Number : 840040, New York
  • Mt. Sinai School of Medicine- Site Number : 840005, New York
  • Columbia University Irving Medical Center- Site Number : 157199, New York
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • NYU Neurogenetics, NYU Langone Medical Center, New York
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.