🔎 Trials Near Me

Gara Jalqabaatti › Dhukkubaa Kuusaa Glycogen Gosa II › North Carolina

Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen Gosa II North Carolina keessatti

Qorannoo 8 Dhukkubaa Kuusaa Glycogen Gosa II f North Carolina keessatti hirmaatuu jiru.

Magaalota North Carolina keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Duke University School of Medicine - Early Phase Research Unit, Durham
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Duke University, Durham
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Pompe Disease Registry Protocol

  • Carolinas Medical Center Hospital- Site Number : 840065, Charlotte
  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease

  • Duke University Medical Center, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT01665326

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Duke University Medical Center, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Cognitive and Neurological Pathologies in Pompe Disease

  • Duke University Medical Center, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 18 · Saalaa hunda · Haaromfame 04-Bit-2026 · NCT04639336

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.