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Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Cincinnati Children's Hospital Medical Center, Cincinnati
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Disease Registry Protocol

  • University of Cincinnati Medical Center- Site Number : 840124, Cincinnati
  • University Hospitals Cleveland Medical Center- Site Number : 840119, Cleveland
  • Cleveland Clinic - Cleveland- Site Number : 840048, Cleveland
  • fi 2 dabalataa
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • LSD Data Registry Site LLC- Site Number : 840094, Dublin
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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • University of Cincinnati Medical Center, Cincinnati
  • Cincinnati Children's Hospital, Cincinnati
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Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.