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Qorannoo 6 Dhukkubaa Kuusaa Glycogen Gosa II f Virginia keessatti hirmaatuu jiru.

Magaalota Virginia keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • The Lysosomal & Rare Disorders Research & Treatment Center, Fairfax
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Virginia Commonwealth University (VCU), Richmond
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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Disease Registry Protocol

  • O & O Alpan- Site Number : 840025, Fairfax
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • O & O Alpan- Site Number : 840025, Fairfax
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Umuriin hundi · Dubartoota · Haaromfame 16-Elb-2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
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Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.