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ATR 1072 in Participants With PRKAG2 Syndrome

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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 18-Ful-2026 · NCT07738107

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Rare Glycogen Storage Diseases Natural History Study

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Umuriin 0 hanga 90 · Saalaa hunda · Haaromfame 07-Ama-2026 · NCT06795152

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

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Umuriin hundi · Saalaa hunda · Haaromfame 29-Cam-2025 · NCT01793168

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.