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Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen North Carolina keessatti
Qorannoo 3 Dhukkubaa Kuusaa Glycogen f North Carolina keessatti hirmaatuu jiru.
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A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Duke University, Durham
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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Duke University Medical Center, Durham
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155Rare Glycogen Storage Diseases Natural History Study
- Duke University, Durham
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Umuriin 0 hanga 90 · Saalaa hunda · Haaromfame 07-Ama-2026 · NCT06795152Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.