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Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen North Carolina keessatti

Qorannoo 3 Dhukkubaa Kuusaa Glycogen f North Carolina keessatti hirmaatuu jiru.

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A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Duke University, Durham
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Rare Glycogen Storage Diseases Natural History Study

  • Duke University, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 90 · Saalaa hunda · Haaromfame 07-Ama-2026 · NCT06795152

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.