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Qorannoo klinikaalii Dogoggora Dhalootaa Metabolizimii California keessatti

Qorannoo 5 Dogoggora Dhalootaa Metabolizimii f California keessatti hirmaatuu jiru.

Magaalota California keessatti

Takkalaa qorannoo (Ingiliffa)

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Namoota walitti qabaa jiraQorannoo ilaalaa
Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Mud-2025 · NCT05295433

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.