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Qorannoo klinikaalii Dogoggora Dhalootaa Metabolizimii California keessatti
Qorannoo 5 Dogoggora Dhalootaa Metabolizimii f California keessatti hirmaatuu jiru.
Magaalota California keessatti
Takkalaa qorannoo (Ingiliffa)
A Long-Term Observational Study of Patients With Fucosidosis
- Children's Hospital of Orange County, Orange
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Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
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Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Ronald Reagan UCLA Medical Center, Los Angeles
- University of Stanford Medical Center, Palo Alto
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
- Ronald Reagan UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital Stanford, Stanford
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Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
- UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital at Stanford, Palo Alto
- Altman Clinical and Translational Research Institution, San Diego
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Mud-2025 · NCT05295433Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.