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Takkalaa qorannoo (Ingiliffa)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
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1 Month – 100 Years · Saalaa hunda · Haaromfame 28-Ful-2026 · NCT02890342A Long-Term Observational Study of Patients With Fucosidosis
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Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400Clinical and Laboratory Study of Methylmalonic Acidemia
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1 Month – 115 Years · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT00078078Study of Alkaptonuria
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Umuriin 2 hanga 115 · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT00005909Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
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7 Months – 15 Months · Saalaa hunda · Haaromfame 31-Hag-2026 · NCT06805695Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
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1 Month – 25 Years · Saalaa hunda · Haaromfame 15-Elb-2026 · NCT06839456Registry of Patients Diagnosed With Lysosomal Storage Diseases
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Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
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Hanga umuriin 30 · Saalaa hunda · Haaromfame 20-Gur-2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
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Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Mud-2025 · NCT05295433Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.