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Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
1 Month – 100 Years · Saalaa hunda · Haaromfame 28-Ful-2026 · NCT02890342

A Long-Term Observational Study of Patients With Fucosidosis

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Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400

Clinical and Laboratory Study of Methylmalonic Acidemia

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1 Month – 115 Years · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT00078078

Study of Alkaptonuria

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Umuriin 2 hanga 115 · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT00005909

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

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7 Months – 15 Months · Saalaa hunda · Haaromfame 31-Hag-2026 · NCT06805695

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Namoota walitti qabaa jiraSadarkaa 1/2
1 Month – 25 Years · Saalaa hunda · Haaromfame 15-Elb-2026 · NCT06839456

Registry of Patients Diagnosed With Lysosomal Storage Diseases

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Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

Namoota walitti qabaa jiraSadarkaa jalqabaa 1
Hanga umuriin 30 · Saalaa hunda · Haaromfame 20-Gur-2026 · NCT02356653

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Mud-2025 · NCT05295433

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.