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Qorannoo klinikaalii Dogoggora Dhalootaa Metabolizimii Pennsylvania keessatti

Qorannoo 6 Dogoggora Dhalootaa Metabolizimii f Pennsylvania keessatti hirmaatuu jiru.

Magaalota Pennsylvania keessatti

Takkalaa qorannoo (Ingiliffa)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
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1 Month – 100 Years · Saalaa hunda · Haaromfame 28-Ful-2026 · NCT02890342

Clinical and Laboratory Study of Methylmalonic Acidemia

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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1 Month – 115 Years · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT00078078

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

  • Children's Hospital of Philadelphia, Philadelphia
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1 Month – 25 Years · Saalaa hunda · Haaromfame 15-Elb-2026 · NCT06839456

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

  • Children's Hospital of Philadelphia, Philadelphia
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Hanga umuriin 30 · Saalaa hunda · Haaromfame 20-Gur-2026 · NCT02356653

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
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Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.