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Uncovering Genes Behind Cartilage Tumors and Vascular Anomalies Using Genomic Sequencing

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Umuriin 2 hanga 100 · Saalaa hunda · Haaromfame 01-Onk-2026 · NCT06749366

Study of Skeletal Disorders

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2 Months – 100 Years · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT05031507

Prospective Clinical Assessment Study in Children With Hypochondroplasia

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30 Months – 16 Years · Saalaa hunda · Haaromfame 16-Ado-2026 · NCT06410976

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

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0 Years – 32 Months · Saalaa hunda · Haaromfame 13-Ado-2026 · NCT07169279

A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating

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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 15-Cam-2026 · NCT07591584

Non-invasive Functional Assessment and Pathogenesis of Morquio A

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Umuriin hundi · Saalaa hunda · Haaromfame 13-Cam-2026 · NCT05284006

Effects of Bisphosphonates on OI-Related Hearing Loss

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Umuriin 6 hanga 100 · Saalaa hunda · Haaromfame 28-Elb-2026 · NCT04152551

Registry of Patients Diagnosed With Lysosomal Storage Diseases

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Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 50 · Dubartoota · Haaromfame 17-Bit-2026 · NCT04532047

Longitudinal Study of Neurodegenerative Disorders

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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

Cardiac Structure and Function in MPS

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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 26-Ama-2026 · NCT07361536

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.