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Gara Jalqabaatti › Mucopolysaccharidosis IV › California

Qorannoo klinikaalii Mucopolysaccharidosis IV California keessatti

Qorannoo 6 Mucopolysaccharidosis IV f California keessatti hirmaatuu jiru.

Takkalaa qorannoo (Ingiliffa)

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • UCSF Benioff Children's Hospital, Oakland
Namoota walitti qabaa jiraQorannoo ilaalaa
30 Months – 16 Years · Saalaa hunda · Haaromfame 16-Ado-2026 · NCT06410976

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

  • UCSF Benioff Children's Hospital, Oakland
Namoota walitti qabaa jiraSadarkaa 2
0 Years – 32 Months · Saalaa hunda · Haaromfame 13-Ado-2026 · NCT07169279

A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating

  • People Science, Los Angeles
Namoota walitti qabaa jiraHojjettoota fayyaa simatamoo
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 15-Cam-2026 · NCT07591584

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Namoota walitti qabaa jiraQorannoo ilaalaa
Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 50 · Dubartoota · Haaromfame 17-Bit-2026 · NCT04532047

Cardiac Structure and Function in MPS

  • Children'S Hospital of Orange County, Orange
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 26-Ama-2026 · NCT07361536

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.