Gara Jalqabaatti › Myotonic Dystrophy › California
Qorannoo klinikaalii Myotonic Dystrophy California keessatti
Qorannoo 5 Myotonic Dystrophy f California keessatti hirmaatuu jiru.
Magaalota California keessatti
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Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- UCSD - Altman Clinical and Translational Research Institute, La Jolla
- UCLA Medical Center (Department of Neurology), Los Angeles
- Stanford Neuroscience Health Center, Palo Alto
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Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of California, San Diego, La Jolla
- University of California, Los Angeles, Los Angeles
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Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT03981575DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- University of California, Los Angeles, Los Angeles
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59 Months · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT05224778Study of ATX-01 in Participants With DM1
- UCLA, Los Angeles
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Umuriin 18 hanga 64 · Saalaa hunda · Haaromfame 10-Gur-2026 · NCT06300307Myotonic Dystrophy Family Registry
- Myotonic Dystrophy Foundation, Oakland
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Umuriin hundi · Saalaa hunda · Haaromfame 21-Sad-2024 · NCT02398786Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.