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Qorannoo klinikaalii Myotonic Dystrophy Ameerikaa Keessatti hirmaatuu

Qorannoo 19 Myotonic Dystrophy f bakka adda addaa Ameerikaa Keessatti hirmaatuu jiru.

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Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

Namoota walitti qabaa jiraSadarkaa 3
Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 04-Ful-2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 3 hanga 17 · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT06747884

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT03981575

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

Namoota walitti qabaa jiraQorannoo ilaalaa
59 Months · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT05224778

Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 17 · Saalaa hunda · Haaromfame 05-Wax-2026 · NCT07630389

Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)

Namoota walitti qabaa jira
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 15-Elb-2026 · NCT06716931

Remote Assessments and Genetic Determinants of Myotonic Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 88 · Saalaa hunda · Haaromfame 01-Elb-2026 · NCT07505342

Study of ATX-01 in Participants With DM1

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 64 · Saalaa hunda · Haaromfame 10-Gur-2026 · NCT06300307

Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 23-Ama-2026 · NCT07362875

Extracellular RNA Biomarkers of Myotonic Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT05020002

Biomarker Development for Muscular Dystrophies

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT05019625

Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT06075693

Long-Term Development of Muscular Dystrophy Outcome Assessments

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 6 hanga 50 · Saalaa hunda · Haaromfame 18-Sad-2025 · NCT05989620

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 15-Onk-2025 · NCT00082108

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 6 hanga 45 · Saalaa hunda · Haaromfame 28-Cam-2025 · NCT05004129

Myotonic Dystrophy Family Registry

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 21-Sad-2024 · NCT02398786

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.