Gara Jalqabaatti › Myotonic Dystrophy › New York
Qorannoo klinikaalii Myotonic Dystrophy New York keessatti
Qorannoo 8 Myotonic Dystrophy f New York keessatti hirmaatuu jiru.
Magaalota New York keessatti
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Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- University of Rochester Medical Center, Rochester
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Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York
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Umuriin 10 hanga 55 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06844214Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of Rochester, Rochester
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Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT03981575DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- University of Rochester Medical Center, Rochester
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59 Months · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT05224778Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
- University of Rochester, Rochester
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Umuriin 0 hanga 17 · Saalaa hunda · Haaromfame 05-Wax-2026 · NCT07630389Remote Assessments and Genetic Determinants of Myotonic Dystrophy
- University of Rochester, Rochester
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Umuriin 18 hanga 88 · Saalaa hunda · Haaromfame 01-Elb-2026 · NCT07505342Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
- University of Rochester Medical Center, Department of Neurology, Rochester
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Umuriin hundi · Saalaa hunda · Haaromfame 15-Onk-2025 · NCT00082108Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
- University of Rochester - Medical Center, Rochester
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Umuriin 6 hanga 45 · Saalaa hunda · Haaromfame 28-Cam-2025 · NCT05004129Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.