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Gara Jalqabaatti › Myotonic Dystrophy › New York

Qorannoo klinikaalii Myotonic Dystrophy New York keessatti

Qorannoo 8 Myotonic Dystrophy f New York keessatti hirmaatuu jiru.

Magaalota New York keessatti

Takkalaa qorannoo (Ingiliffa)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • University of Rochester Medical Center, Rochester
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 10 hanga 55 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06844214

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • University of Rochester, Rochester
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT03981575

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • University of Rochester Medical Center, Rochester
Namoota walitti qabaa jiraQorannoo ilaalaa
59 Months · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT05224778

Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy

  • University of Rochester, Rochester
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 17 · Saalaa hunda · Haaromfame 05-Wax-2026 · NCT07630389

Remote Assessments and Genetic Determinants of Myotonic Dystrophy

  • University of Rochester, Rochester
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 88 · Saalaa hunda · Haaromfame 01-Elb-2026 · NCT07505342

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

  • University of Rochester Medical Center, Department of Neurology, Rochester
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 15-Onk-2025 · NCT00082108

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

  • University of Rochester - Medical Center, Rochester
Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 6 hanga 45 · Saalaa hunda · Haaromfame 28-Cam-2025 · NCT05004129

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.