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Qorannoo klinikaalii Myotonic Dystrophy North Carolina keessatti

Qorannoo 4 Myotonic Dystrophy f North Carolina keessatti hirmaatuu jiru.

Takkalaa qorannoo (Ingiliffa)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • Rare Disease Research, LLC, Hillsborough
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Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
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Umuriin 4 hanga 18 · Dhiroota · Haaromfame 27-Cam-2026 · NCT07608432

Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy

  • Wake Forest University Health Sciences, Winston-Salem
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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 23-Ama-2026 · NCT07362875

Biomarker Development for Muscular Dystrophies

  • Wake Forest University, Winston-Salem
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Umuriin 5 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT05019625

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.