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Gara Jalqabaatti › Myotonic Dystrophy › Pennsylvania

Qorannoo klinikaalii Myotonic Dystrophy Pennsylvania keessatti

Qorannoo 3 Myotonic Dystrophy f Pennsylvania keessatti hirmaatuu jiru.

Takkalaa qorannoo (Ingiliffa)

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Penn Medicine: University of Pennsylvania Health System- Site Number : 8400009, Philadelphia
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 10 hanga 55 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06844214

Biomarker Development for Muscular Dystrophies

  • University of Pittsburgh, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT05019625

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

  • University of Pittsburgh Medical Center, Pittsburgh
Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 6 hanga 45 · Saalaa hunda · Haaromfame 28-Cam-2025 · NCT05004129

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.