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Gara Jalqabaatti › Myotonic Dystrophy › Virginia

Qorannoo klinikaalii Myotonic Dystrophy Virginia keessatti

Qorannoo 8 Myotonic Dystrophy f Virginia keessatti hirmaatuu jiru.

Magaalota Virginia keessatti

Takkalaa qorannoo (Ingiliffa)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • Virginia Commonwealth University - Biotech One, Richmond
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 10 hanga 55 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06844214

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

  • Virginia Commonwealth University, Richmond
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 04-Ful-2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

  • Virginia Commonwealth University, Richmond
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 3 hanga 17 · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT06747884

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • Virginia Commonwealth University, Richmond
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT03981575

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • Virginia Commonwealth University, Richmond
Namoota walitti qabaa jiraQorannoo ilaalaa
59 Months · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT05224778

Study of ATX-01 in Participants With DM1

  • Virginia Commonwealth University, Richmond
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 64 · Saalaa hunda · Haaromfame 10-Gur-2026 · NCT06300307

Long-Term Development of Muscular Dystrophy Outcome Assessments

  • Virginia Commonwealth University, Richmond
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 6 hanga 50 · Saalaa hunda · Haaromfame 18-Sad-2025 · NCT05989620

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.