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Qorannoo klinikaalii Myotonic Dystrophy Virginia keessatti
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Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- Virginia Commonwealth University - Biotech One, Richmond
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Umuriin 16 fi ol · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
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Umuriin 10 hanga 55 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06844214Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
- Virginia Commonwealth University, Richmond
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Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 04-Ful-2026 · NCT07700225Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
- Virginia Commonwealth University, Richmond
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Umuriin 3 hanga 17 · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT06747884Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- Virginia Commonwealth University, Richmond
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Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT03981575DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- Virginia Commonwealth University, Richmond
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59 Months · Saalaa hunda · Haaromfame 10-Wax-2026 · NCT05224778Study of ATX-01 in Participants With DM1
- Virginia Commonwealth University, Richmond
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Umuriin 18 hanga 64 · Saalaa hunda · Haaromfame 10-Gur-2026 · NCT06300307Long-Term Development of Muscular Dystrophy Outcome Assessments
- Virginia Commonwealth University, Richmond
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Umuriin 6 hanga 50 · Saalaa hunda · Haaromfame 18-Sad-2025 · NCT05989620Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.