Gara Jalqabaatti › Dhibee Pelizaeus-Merzbacher
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Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
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6 Months – 17 Years · Dhiroota · Haaromfame 02-Onk-2026 · NCT05659901UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
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1 Week – 22 Years · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT02254863Longitudinal Study of Neurodegenerative Disorders
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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
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Umuriin 2 hanga 17 · Dhiroota · Haaromfame 12-Mud-2025 · NCT06150716The Myelin Disorders Biorepository Project
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.