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Gara Jalqabaatti › Dhibee Pelizaeus-Merzbacher › Pennsylvania

Qorannoo klinikaalii Dhibee Pelizaeus-Merzbacher Pennsylvania keessatti

Qorannoo 4 Dhibee Pelizaeus-Merzbacher f Pennsylvania keessatti hirmaatuu jiru.

Magaalota Pennsylvania keessatti

Takkalaa qorannoo (Ingiliffa)

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

  • Ionis Investigative Site, Philadelphia
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6 Months – 17 Years · Dhiroota · Haaromfame 02-Onk-2026 · NCT05659901

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

  • Ionis Investigative Site, Philadelphia
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Umuriin 2 hanga 17 · Dhiroota · Haaromfame 12-Mud-2025 · NCT06150716

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.