Gara Jalqabaatti › Dhibee Pelizaeus-Merzbacher › Pennsylvania
Qorannoo klinikaalii Dhibee Pelizaeus-Merzbacher Pennsylvania keessatti
Qorannoo 4 Dhibee Pelizaeus-Merzbacher f Pennsylvania keessatti hirmaatuu jiru.
Magaalota Pennsylvania keessatti
Takkalaa qorannoo (Ingiliffa)
Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
- Ionis Investigative Site, Philadelphia
Namoota walitti qabaa jiraQorannoo ilaalaa
6 Months – 17 Years · Dhiroota · Haaromfame 02-Onk-2026 · NCT05659901Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
- Ionis Investigative Site, Philadelphia
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 2 hanga 17 · Dhiroota · Haaromfame 12-Mud-2025 · NCT06150716The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.