Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › Arkansas
Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Arkansas keessatti
Qorannoo 4 Atrophy Muscular Sirna Caddii f Arkansas keessatti hirmaatuu jiru.
Magaalota Arkansas keessatti
Takkalaa qorannoo (Ingiliffa)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 31-Ama-2025 · NCT04174157Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.