Gara Jalqabaatti › Atrophy Muscular Sirna Caddii
Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Ameerikaa Keessatti hirmaatuu
Qorannoo 23 Atrophy Muscular Sirna Caddii f bakka adda addaa Ameerikaa Keessatti hirmaatuu jiru.
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Takkalaa qorannoo (Ingiliffa)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
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Umuriin 15 hanga 60 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT07444476A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
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Hanga umuriin 2 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT07047144A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
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3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986A Registry of Cases of Spinal Muscular Atrophy
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Umuriin hundi · Saalaa hunda · Haaromfame 30-Ful-2026 · NCT07805278ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
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Umuriin 2 hanga 100 · Saalaa hunda · Haaromfame 18-Ful-2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
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Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
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Umuriin 18 hanga 80 · Saalaa hunda · Haaromfame 02-Ful-2026 · NCT07521930Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Namoota walitti qabaa jira
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Namoota walitti qabaa jiraSadarkaa 3
0 Days – 42 Days · Saalaa hunda · Haaromfame 18-Hag-2026 · NCT07221669A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec
Namoota walitti qabaa jiraSadarkaa 3
0 Days – 7 Months · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT07444450Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
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Umuriin 5 hanga 20 · Saalaa hunda · Haaromfame 09-Ado-2026 · NCT06532474Clinical Procedures to Support Research in ALS
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 15-Wax-2026 · NCT03489278ALS/MND Natural History Study Data Repository
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Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 20-Cam-2026 · NCT05966038Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 14-Cam-2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
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Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT07488338Gait and Bone Health in SMA
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Umuriin 8 hanga 50 · Saalaa hunda · Haaromfame 18-Bit-2026 · NCT07400198Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 17-Bit-2026 · NCT07478172A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
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Umuriin 18 hanga 54 · Dubartoota · Haaromfame 09-Bit-2026 · NCT05789758Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 16-Ama-2026 · NCT07223489Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 31-Ama-2025 · NCT04174157Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.