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Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › Colorado

Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Colorado keessatti

Qorannoo 4 Atrophy Muscular Sirna Caddii f Colorado keessatti hirmaatuu jiru.

Magaalota Colorado keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital Colorado, Aurora
Namoota walitti qabaa jiraSadarkaa 2
Hanga umuriin 2 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Hospital of Colorado, Aurora
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Hospital of Colorado, Aurora
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT05861999

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital Colorado, Aurora
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 31-Ama-2025 · NCT04174157

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.