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Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Georgia keessatti
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A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Healthcare of Atlanta, Atlanta
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Hanga umuriin 2 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT07047144A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
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3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
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3 Months – 24 Months · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT05861999Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.