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Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › Illinois

Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Illinois keessatti

Qorannoo 6 Atrophy Muscular Sirna Caddii f Illinois keessatti hirmaatuu jiru.

Magaalota Illinois keessatti

Takkalaa qorannoo (Ingiliffa)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Ann and Robert H. Lurie Children Hospital of Chicago, Chicago
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Lurie Childrens Hospital, Chicago
Namoota walitti qabaa jira
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago
Namoota walitti qabaa jiraSadarkaa 3
0 Days – 42 Days · Saalaa hunda · Haaromfame 18-Hag-2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Northwestern University, Chicago
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 20-Cam-2026 · NCT05966038

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.