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Studii clinice pentru Atrofie musculară spinală în California
11 studii pentru Atrofie musculară spinală caută participanți în California.
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A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Stanford University Medical Center, Palo Alto
În curs de recrutareFaza 3
Vârste de la 15 la 60 · Toate sexele · Actualizat 2 oct. 2026 · NCT07444476A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Hospital of Orange County (CHOC), Orange
- Stanford Neuroscience Health Center (SNHC), Palo Alto
În curs de recrutareFaza 2
Până la vârsta de 2 · Toate sexele · Actualizat 2 oct. 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Stanford University Medical Center, Stanford
În curs de recrutareFaza 2
Vârste de la 5 la 17 · Toate sexele · Actualizat 14 sept. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Valley Children's Hospital, Madera
- Stanford Univ Medical Center, Palo Alto
În curs de recrutareFaza 4
3 Months – 24 Months · Toate sexele · Actualizat 10 sept. 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Children's Hospital of Orange County, Orange
- Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
În curs de recrutareFaza 1
Vârste de 3 ani și peste · Toate sexele · Actualizat 3 sept. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Children's Hospital Orange County, Orange
- Stanford Medical Center, Palo Alto
- Rady Children's Hospital, San Diego
În curs de recrutare
Vârste de 3 ani și peste · Toate sexele · Actualizat 19 aug. 2026 · NCT05866419Clinical Procedures to Support Research in ALS
- University of California, Irvine, Irvine
- Stanford University, Palo Alto
- California Pacific Medical Center, San Francisco
În curs de recrutareStudiu observațional
Vârste de 18 ani și peste · Toate sexele · Actualizat 15 iun. 2026 · NCT03489278ALS/MND Natural History Study Data Repository
- Loma Linda University Health, Loma Linda
- Kaiser Permanente, Los Angeles
În curs de recrutareStudiu observațional
Vârste de la 18 la 90 · Toate sexele · Actualizat 20 mai 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
În curs de recrutareStudiu observaționalVoluntari sănătoși bineveniți
Vârste de 5 ani și peste · Toate sexele · Actualizat 9 apr. 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Stanford Neuroscience Health Center, Palo Alto
În curs de recrutareStudiu observațional
Vârste de la 18 la 54 · Femei · Actualizat 9 mar. 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Children's Hospital of Los Angeles, Los Angeles
- University of California Los Angeles Health, Los Angeles
- Valley Children's Healthcare, Madera
- și încă 3
În curs de recrutareStudiu observațional
Toate vârstele · Toate sexele · Actualizat 31 ian. 2025 · NCT04174157Sursă: ClinicalTrials.gov, date preluate la 6 oct. 2026. Fiecare studiu are propriile criterii de eligibilitate; echipa de cercetare decide cine poate participa.