🔎 Trials Near Me

Acasă › Atrofie musculară spinală › Texas

Studii clinice pentru Atrofie musculară spinală în Texas

10 studii pentru Atrofie musculară spinală caută participanți în Texas.

Orașe în Texas

Text oficial al studiului (în engleză)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • The University of Texas Southwestern Medical Center at Dallas, Dallas
  • Cook Children's Jane and John Justin Neurosciences Center, Fort Worth
În curs de recrutareFaza 4
3 Months – 24 Months · Toate sexele · Actualizat 2 oct. 2026 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • University of Texas Southwestern Medical Center, Dallas
  • Neurology Rare Disease Center, Flower Mound
  • Cook Children's Medical Center, Fort Worth
  • și încă 1
În curs de recrutareFaza 2
Până la vârsta de 2 · Toate sexele · Actualizat 2 oct. 2026 · NCT07047144

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Neurology Rare Disease Center, Flower Mound
  • Texas Children's Hospital, Houston
În curs de recrutareFaza 2
Vârste de la 5 la 17 · Toate sexele · Actualizat 14 sept. 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Texas Southwestern Medical Center, Dallas
În curs de recrutareFaza 4
3 Months – 24 Months · Toate sexele · Actualizat 10 sept. 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Texas Childrens Hospital Houston, Houston
În curs de recrutareFaza 1
Vârste de 3 ani și peste · Toate sexele · Actualizat 3 sept. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Texas Children's Hospital, Houston
În curs de recrutare
Vârste de 3 ani și peste · Toate sexele · Actualizat 19 aug. 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Neurology Rare Disease Center, Flower Mound
În curs de recrutareFaza 3
0 Days – 42 Days · Toate sexele · Actualizat 18 aug. 2026 · NCT07221669

A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec

  • Neurology Rare Disease Center, Flower Mound
În curs de recrutareFaza 3
0 Days – 7 Months · Toate sexele · Actualizat 11 aug. 2026 · NCT07444450

Clinical Procedures to Support Research in ALS

  • University of Texas San Antonio Health Science Center, San Antonio
În curs de recrutareStudiu observațional
Vârste de 18 ani și peste · Toate sexele · Actualizat 15 iun. 2026 · NCT03489278

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Cook Children's, Fort Worth
  • Texas Children's Hospital, Houston
  • CHRISTUS Health, San Antonio
În curs de recrutareStudiu observațional
Toate vârstele · Toate sexele · Actualizat 31 ian. 2025 · NCT04174157

Sursă: ClinicalTrials.gov, date preluate la 5 oct. 2026. Fiecare studiu are propriile criterii de eligibilitate; echipa de cercetare decide cine poate participa.