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Klinické štúdie Srpkovitá anémie v štáte Kalifornia

18 štúdií pre Srpkovitá anémie hľadá účastníkov v zariadeniach v štáte Kalifornia.

Mestá v štáte Kalifornia

Oficiálny text štúdie (anglicky)

Exercise in Child Health

  • University of California, Irvine, Irvine
Prebieha náborVítaní zdravých dobrovoľníkov
Vek 10 až 17 · Všetky pohlavia · Aktualizované 2. 10. 2026 · NCT05359991

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  • Ctr for Inherited Blood Disorders, Orange
Prebieha náborFáza 3
Vek 12 až 100 · Všetky pohlavia · Aktualizované 28. 9. 2026 · NCT06439082

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Children's Hospital Los Angeles - Endocrinology, Los Angeles
  • UCSF Oakland Benioff ChildHosp, Oakland
Prebieha náborFáza 3
Vek 2 a viac · Všetky pohlavia · Aktualizované 18. 9. 2026 · NCT06609226

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

  • Children's Hospital Los Angeles - Endocrinology, Los Angeles
  • Valley Children's Hospital, Madera
  • Stanford University_Palo Alto, Palo Alto
  • a 1 ďalších
Prebieha náborFáza 3
Vek 12 a viac · Všetky pohlavia · Aktualizované 17. 9. 2026 · NCT06612268

Sub-dissociative Dose Ketamine in Treatment of Vaso-occlusive Pain Event in Children and Young Adults

  • Harbor UCLA Medical Center, Torrance
Prebieha náborFáza 2
Vek 5 až 20 · Všetky pohlavia · Aktualizované 2. 9. 2026 · NCT07369024

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

  • University of California San Diego - La Jolla, La Jolla
  • UCSF Benioff Children's Hospital Oakland, Oakland
Prebieha náborFáza 1/2Vítaní zdravých dobrovoľníkov
Vek 18 a viac · Všetky pohlavia · Aktualizované 18. 8. 2026 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • a 5 ďalších
Prebieha náborObservačná štúdia
Všetky vekové kategórie · Všetky pohlavia · Aktualizované 17. 8. 2026 · NCT04398628

Safety, Efficacy, and Pharmacokinetics of CSL889 in Adults and Adolescents With Sickle Cell Disease During Vaso-Occlusive Crisis

  • Univ. of California, San Francisco Health Care, Oakland
  • University of California Irvine, Orange
Prebieha náborFáza 2
Vek 12 a viac · Všetky pohlavia · Aktualizované 14. 8. 2026 · NCT06699849

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • University of California Irvine, Orange
Prebieha náborFáza 2
Vek 18 a viac · Všetky pohlavia · Aktualizované 5. 8. 2026 · NCT07224360

The Efficacy and Safety of Rilzabrutinib in Participants Aged 10 to 65 Years With Sickle-cell Disease

  • University of California San Francisco- Site Number : 8400040, Fresno
Prebieha náborFáza 3
Vek 10 až 65 · Všetky pohlavia · Aktualizované 29. 7. 2026 · NCT06975865

Myeloablative Conditioning, Prophylactic Defibrotide and Haplo AlloSCT for Patients With Sickle Cell Disease

  • University of California Los Angeles, Los Angeles
Prebieha náborFáza 2
6 Months – 21 Years · Všetky pohlavia · Aktualizované 27. 7. 2026 · NCT02675959

Alendronate for Osteonecrosis in Adults With Sickle Cell Disease

  • UC Davis Comprehensive Cancer Center, Sacramento
Prebieha náborFáza 2
Vek 18 až 80 · Všetky pohlavia · Aktualizované 16. 7. 2026 · NCT06016634

Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease

  • Children's Hospital Los Angeles, Los Angeles
  • Lucile Packard Children's Hospital, Palo Alto
Prebieha náborFáza 1/2
Vek 12 až 50 · Všetky pohlavia · Aktualizované 2. 7. 2026 · NCT04819841

Haploidentical Transplantation With Pre-Transplant Immunosuppressive Therapy for Patients With Sickle Cell Disease

  • City of Hope Medical Center, Duarte
Prebieha náborFáza 1
Vek 1 až 30 · Všetky pohlavia · Aktualizované 12. 5. 2026 · NCT03279094

Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients With Severe Sickle Cell Disease

  • University of California, Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
Prebieha náborFáza 1/2
Vek 12 až 35 · Všetky pohlavia · Aktualizované 16. 4. 2026 · NCT04774536

Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial

  • UCSF Benioff Children's Hospital Oakland, Oakland
Prebieha náborFáza 2
Vek 15 až 40 · Všetky pohlavia · Aktualizované 13. 3. 2026 · NCT06260891

Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain

  • UCLA Mattel Children's Hospital Ronald Reagan Hospital, Los Angeles
Prebieha nábor
Vek 16 až 30 · Všetky pohlavia · Aktualizované 7. 1. 2026 · NCT06374238

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

  • University of California, San Francisco (UCSF), Oakland
Prebieha náborObservačná štúdia
Vek 18 a viac · Všetky pohlavia · Aktualizované 22. 6. 2025 · NCT06385886

Z ClinicalTrials.gov, dáta načítané 5. 10. 2026. Každá štúdia má vlastné kritériá oprávnenosti; tím štúdie rozhoduje o účasti.