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Klinične študije za Srpastocelična anemija v Kalifornija

18 študij za Srpastocelična anemija išče udeležence na lokacijah v Kalifornija.

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Uradno besedilo študije (angleško)

Exercise in Child Health

  • University of California, Irvine, Irvine
Vključevanje udeležencevVabljeni zdravi prostovoljci
Starost 10–17 · Vsi spoli · Posodobljeno 2. okt. 2026 · NCT05359991

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  • Ctr for Inherited Blood Disorders, Orange
Vključevanje udeležencevFaza 3
Starost 12–100 · Vsi spoli · Posodobljeno 28. sep. 2026 · NCT06439082

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Children's Hospital Los Angeles - Endocrinology, Los Angeles
  • UCSF Oakland Benioff ChildHosp, Oakland
Vključevanje udeležencevFaza 3
Starost 2 in več · Vsi spoli · Posodobljeno 18. sep. 2026 · NCT06609226

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

  • Children's Hospital Los Angeles - Endocrinology, Los Angeles
  • Valley Children's Hospital, Madera
  • Stanford University_Palo Alto, Palo Alto
  • in še 1
Vključevanje udeležencevFaza 3
Starost 12 in več · Vsi spoli · Posodobljeno 17. sep. 2026 · NCT06612268

Sub-dissociative Dose Ketamine in Treatment of Vaso-occlusive Pain Event in Children and Young Adults

  • Harbor UCLA Medical Center, Torrance
Vključevanje udeležencevFaza 2
Starost 5–20 · Vsi spoli · Posodobljeno 2. sep. 2026 · NCT07369024

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

  • University of California San Diego - La Jolla, La Jolla
  • UCSF Benioff Children's Hospital Oakland, Oakland
Vključevanje udeležencevFaza 1/2Vabljeni zdravi prostovoljci
Starost 18 in več · Vsi spoli · Posodobljeno 18. avg. 2026 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • in še 5
Vključevanje udeležencevOpazovalna študija
Vse starosti · Vsi spoli · Posodobljeno 17. avg. 2026 · NCT04398628

Safety, Efficacy, and Pharmacokinetics of CSL889 in Adults and Adolescents With Sickle Cell Disease During Vaso-Occlusive Crisis

  • Univ. of California, San Francisco Health Care, Oakland
  • University of California Irvine, Orange
Vključevanje udeležencevFaza 2
Starost 12 in več · Vsi spoli · Posodobljeno 14. avg. 2026 · NCT06699849

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • University of California Irvine, Orange
Vključevanje udeležencevFaza 2
Starost 18 in več · Vsi spoli · Posodobljeno 5. avg. 2026 · NCT07224360

The Efficacy and Safety of Rilzabrutinib in Participants Aged 10 to 65 Years With Sickle-cell Disease

  • University of California San Francisco- Site Number : 8400040, Fresno
Vključevanje udeležencevFaza 3
Starost 10–65 · Vsi spoli · Posodobljeno 29. jul. 2026 · NCT06975865

Myeloablative Conditioning, Prophylactic Defibrotide and Haplo AlloSCT for Patients With Sickle Cell Disease

  • University of California Los Angeles, Los Angeles
Vključevanje udeležencevFaza 2
6 Months – 21 Years · Vsi spoli · Posodobljeno 27. jul. 2026 · NCT02675959

Alendronate for Osteonecrosis in Adults With Sickle Cell Disease

  • UC Davis Comprehensive Cancer Center, Sacramento
Vključevanje udeležencevFaza 2
Starost 18–80 · Vsi spoli · Posodobljeno 16. jul. 2026 · NCT06016634

Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease

  • Children's Hospital Los Angeles, Los Angeles
  • Lucile Packard Children's Hospital, Palo Alto
Vključevanje udeležencevFaza 1/2
Starost 12–50 · Vsi spoli · Posodobljeno 2. jul. 2026 · NCT04819841

Haploidentical Transplantation With Pre-Transplant Immunosuppressive Therapy for Patients With Sickle Cell Disease

  • City of Hope Medical Center, Duarte
Vključevanje udeležencevFaza 1
Starost 1–30 · Vsi spoli · Posodobljeno 12. maj 2026 · NCT03279094

Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients With Severe Sickle Cell Disease

  • University of California, Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
Vključevanje udeležencevFaza 1/2
Starost 12–35 · Vsi spoli · Posodobljeno 16. apr. 2026 · NCT04774536

Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial

  • UCSF Benioff Children's Hospital Oakland, Oakland
Vključevanje udeležencevFaza 2
Starost 15–40 · Vsi spoli · Posodobljeno 13. mar. 2026 · NCT06260891

Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain

  • UCLA Mattel Children's Hospital Ronald Reagan Hospital, Los Angeles
Vključevanje udeležencev
Starost 16–30 · Vsi spoli · Posodobljeno 7. jan. 2026 · NCT06374238

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

  • University of California, San Francisco (UCSF), Oakland
Vključevanje udeležencevOpazovalna študija
Starost 18 in več · Vsi spoli · Posodobljeno 22. jun. 2025 · NCT06385886

Vir: ClinicalTrials.gov, podatki pridobljeni 5. okt. 2026. Vsaka študija ima svoje pogoje vključitve; ekipa študije odloči, kdo lahko sodeluje.