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Klinične študije za Srpastocelična anemija v Philadelphia, PA

15 študij za Srpastocelična anemija išče udeležence na lokacijah v Philadelphia in okolici (v razdalji približno 30 milj). Odprite študijo, da vidite, kdo lahko sodeluje in kako kontaktirati ekipo.

Uradno besedilo študije (angleško)

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A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

Vključevanje udeležencevFaza 3
  • Thomas Jefferson University Me, Philadelphia
Starost 12–100 · Vsi spoli · Posodobljeno 28. sep. 2026 · NCT06439082

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

Vključevanje udeležencevFaza 3
  • Children's Hosptl Philadelphia, Philadelphia
  • St Christopher Hosp for Child, Philadelphia
  • Nemours/AI duPont Hosp-Chld, Wilmington · 25 mi stran
Starost 12 in več · Vsi spoli · Posodobljeno 17. sep. 2026 · NCT06612268

A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease

Vključevanje udeležencevFaza 1/2Vabljeni zdravi prostovoljci
  • Childrens Hospital Of Philadelphia, Philadelphia
Starost 12–55 · Vsi spoli · Posodobljeno 9. sep. 2026 · NCT06546670

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

Vključevanje udeležencevFaza 1/2Vabljeni zdravi prostovoljci
  • Local Institution - 0029, Philadelphia
  • Thomas Jefferson University - Medicine/GI and Hepatology, Philadelphia
Starost 18 in več · Vsi spoli · Posodobljeno 18. avg. 2026 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

Vključevanje udeležencevOpazovalna študija
  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • in še 1
Vse starosti · Vsi spoli · Posodobljeno 17. avg. 2026 · NCT04398628

Empowering Adolescents and Young Adults With Sickle Cell Disease as Partners in Treatment Decision Making (EMPOWER-AYA)

Vključevanje udeležencev
  • Nemours Children's Hospital, Delaware, Wilmington · 25 mi stran
Starost 15 in več · Vsi spoli · Posodobljeno 16. jun. 2026 · NCT05383911

Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease

Vključevanje udeležencevOpazovalna študija
  • Children's Hospital of Philadelphia (MRD-HCT), Philadelphia
  • Nemours Children's Hospital, Delaware (MRD-HCT), Wilmington · 25 mi stran
Starost 3–20 · Vsi spoli · Posodobljeno 4. jun. 2026 · NCT06941389

Ruxolitinib-Enhanced Haplo HCT for Children and Young Adults With Sickle Cell Disease

Vključevanje udeležencevFaza 1/2
  • Children's Hospital of Philadelphia, Philadelphia
Starost 12–45 · Vsi spoli · Posodobljeno 4. jun. 2026 · NCT07252050

Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders

Vključevanje udeležencevFaza 1/2
  • Nemours Children's Health, Wilmington · 25 mi stran
1 Day – 21 Years · Vsi spoli · Posodobljeno 29. maj 2026 · NCT03128996

Clinical and Biomarker Effects of Depot Medroxyprogesterone Acetate in Females With Sickle Cell Disease

Vključevanje udeležencevFaza 4
  • Children's Hospital of Philadelphia, Philadelphia
Starost 18–50 · Ženske · Posodobljeno 28. maj 2026 · NCT06665997

A Socio-ecological Approach for Improving Self-management in Adolescents With SCD

Vključevanje udeležencev
  • Children's Hospital of Philadelphia, Philadelphia
  • Nemours Children's Health, Wilmington · 25 mi stran
Starost 13–21 · Vsi spoli · Posodobljeno 11. maj 2026 · NCT06290401

Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial

Vključevanje udeležencevFaza 2
  • Children's Hospital of Philadelphia, Philadelphia
  • Thomas Jefferson University Hospital, Philadelphia
Starost 15–40 · Vsi spoli · Posodobljeno 13. mar. 2026 · NCT06260891

Stress Management and Mindfulness Intervention for Patients With Sickle Cell Disease

Vključevanje udeležencev
  • University of Pennsylvania, Philadelphia
Starost 18 in več · Vsi spoli · Posodobljeno 27. feb. 2026 · NCT07316478

A Long-term Follow-up Study in Patients Who Received BEAM-101

Vključevanje udeležencevOpazovalna študija
  • Children's Hospital of Philadelphia, Philadelphia
Starost 14–37 · Vsi spoli · Posodobljeno 28. jan. 2026 · NCT07373639

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

Vključevanje udeležencevOpazovalna študija
  • University of Pennsylvania, Philadelphia
Starost 18 in več · Vsi spoli · Posodobljeno 22. jun. 2025 · NCT06385886

Študije za Srpastocelična anemija v drugih mestih

Druge študije v Philadelphia

Vir: ClinicalTrials.gov, podatki pridobljeni 6. okt. 2026. Vsaka študija ima svoje pogoje vključitve; ekipa študije odloči, kdo lahko sodeluje.