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Klinične študije za Spinalna mišična atrofija v Kalifornija

11 študij za Spinalna mišična atrofija išče udeležence na lokacijah v Kalifornija.

Mesta v Kalifornija

Uradno besedilo študije (angleško)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
Vključevanje udeležencevFaza 2
Do 2 let · Vsi spoli · Posodobljeno 2. okt. 2026 · NCT07047144

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Stanford University Medical Center, Stanford
Vključevanje udeležencevFaza 2
Starost 5–17 · Vsi spoli · Posodobljeno 14. sep. 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Valley Children's Hospital, Madera
  • Stanford Univ Medical Center, Palo Alto
Vključevanje udeležencevFaza 4
3 Months – 24 Months · Vsi spoli · Posodobljeno 10. sep. 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
Vključevanje udeležencevFaza 1
Starost 3 in več · Vsi spoli · Posodobljeno 3. sep. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Vključevanje udeležencev
Starost 3 in več · Vsi spoli · Posodobljeno 19. avg. 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
Vključevanje udeležencevOpazovalna študija
Starost 18 in več · Vsi spoli · Posodobljeno 15. jun. 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
Vključevanje udeležencevOpazovalna študija
Starost 18–90 · Vsi spoli · Posodobljeno 20. maj 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Vključevanje udeležencevOpazovalna študijaVabljeni zdravi prostovoljci
Starost 5 in več · Vsi spoli · Posodobljeno 9. apr. 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
Vključevanje udeležencevOpazovalna študija
Starost 18–54 · Ženske · Posodobljeno 9. mar. 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • in še 3
Vključevanje udeležencevOpazovalna študija
Vse starosti · Vsi spoli · Posodobljeno 31. jan. 2025 · NCT04174157

Vir: ClinicalTrials.gov, podatki pridobljeni 5. okt. 2026. Vsaka študija ima svoje pogoje vključitve; ekipa študije odloči, kdo lahko sodeluje.