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Kliničke studije za Spinalna mišićna atrofija u državi Kalifornija

11 studija za Spinalna mišićna atrofija traži učesnike na lokacijama u državi Kalifornija.

Gradovi u državi Kalifornija

Zvanični tekst studije (na engleskom)

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

  • Stanford University Medical Center, Palo Alto
Тражи се учесникФаза 3
Узраст од 15 до 60 · Оба пола · Ажурирано 13. 11. 2026. · NCT07444476

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
Тражи се учесникОпсервациона студија
Узраст од 18 до 54 · Жене · Ажурирано 12. 11. 2026. · NCT05789758

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Тражи се учесник
Узраст 3 и старији · Оба пола · Ажурирано 9. 11. 2026. · NCT05866419

ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

  • Stanford Hospital, Stanford
Тражи се учесникФаза 4
Узраст од 2 до 100 · Оба пола · Ажурирано 29. 10. 2026. · NCT07448610

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Stanford University Medical Center, Stanford
Тражи се учесникФаза 2
Узраст од 5 до 17 · Оба пола · Ажурирано 8. 10. 2026. · NCT07287982

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
Тражи се учесникФаза 2
До 2 година · Оба пола · Ажурирано 2. 10. 2026. · NCT07047144

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
Тражи се учесникФаза 1
Узраст 3 и старији · Оба пола · Ажурирано 3. 9. 2026. · NCT06555419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
Тражи се учесникОпсервациона студија
Узраст 18 и старији · Оба пола · Ажурирано 15. 6. 2026. · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
Тражи се учесникОпсервациона студија
Узраст од 18 до 90 · Оба пола · Ажурирано 20. 5. 2026. · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Тражи се учесникОпсервациона студијаЗдраве особе су добродошле
Узраст 5 и старији · Оба пола · Ажурирано 9. 4. 2026. · NCT06839469

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • и још 3
Тражи се учесникОпсервациона студија
Сви узрасти · Оба пола · Ажурирано 31. 1. 2025. · NCT04174157

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.