Почетна › Spinalna mišićna atrofija › Masachuset
Kliničke studije za Spinalna mišićna atrofija u državi Masachuset
8 studija za Spinalna mišićna atrofija traži učesnike na lokacijama u državi Masachuset.
Gradovi u državi Masachuset
Zvanični tekst studije (na engleskom)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Massachusetts General Hospital, Boston
Тражи се учесникФаза 3
Узраст од 15 до 60 · Оба пола · Ажурирано 13. 11. 2026. · NCT07444476A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
Тражи се учесникОпсервациона студија
Узраст од 18 до 54 · Жене · Ажурирано 12. 11. 2026. · NCT05789758Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Тражи се учесник
Узраст 3 и старији · Оба пола · Ажурирано 9. 11. 2026. · NCT05866419ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Boston Childrens Hospital, Boston
Тражи се учесникФаза 4
Узраст од 2 до 100 · Оба пола · Ажурирано 29. 10. 2026. · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Тражи се учесникФаза 2
Узраст од 5 до 17 · Оба пола · Ажурирано 8. 10. 2026. · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
Тражи се учесникФаза 1
Узраст 3 и старији · Оба пола · Ажурирано 3. 9. 2026. · NCT06555419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
Тражи се учесникОпсервациона студија
Узраст од 18 до 90 · Оба пола · Ажурирано 20. 5. 2026. · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
Тражи се учесникОпсервациона студијаЗдраве особе су добродошле
Узраст 5 и старији · Оба пола · Ажурирано 9. 4. 2026. · NCT06839469Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.