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Kliničke studije za Spinalna mišićna atrofija u gradu Boston, MA

7 studija za Spinalna mišićna atrofija traži učesnike na lokacijama u gradu Boston i okolini (u krugu od oko 30 milja). Otvorite studiju da biste videli ko može da učestvuje i kako kontaktirati tim studije.

Zvanični tekst studije (na engleskom)

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A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

Тражи се учесникФаза 3
  • Massachusetts General Hospital, Boston
Узраст од 15 до 60 · Оба пола · Ажурирано 13. 11. 2026. · NCT07444476

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

Тражи се учесникОпсервациона студија
  • Boston Children's Hospital, Boston
Узраст од 18 до 54 · Жене · Ажурирано 12. 11. 2026. · NCT05789758

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Тражи се учесник
  • Boston Children's Hospital, Boston
Узраст 3 и старији · Оба пола · Ажурирано 9. 11. 2026. · NCT05866419

ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

Тражи се учесникФаза 4
  • Boston Childrens Hospital, Boston
Узраст од 2 до 100 · Оба пола · Ажурирано 29. 10. 2026. · NCT07448610

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Тражи се учесникФаза 2
  • Boston Children's Hospital, Boston
Узраст од 5 до 17 · Оба пола · Ажурирано 8. 10. 2026. · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Тражи се учесникФаза 1
  • Boston Children's Hospital, Boston
Узраст 3 и старији · Оба пола · Ажурирано 3. 9. 2026. · NCT06555419

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Тражи се учесникОпсервациона студијаЗдраве особе су добродошле
  • Boston Children's Hospital, Boston
Узраст 5 и старији · Оба пола · Ажурирано 9. 4. 2026. · NCT06839469

Studije za Spinalna mišićna atrofija u drugim gradovima

Ostale studije u gradu Boston

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.