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Kliničke studije za Spinalna mišićna atrofija u državi Тексас

8 studija za Spinalna mišićna atrofija traži učesnike na lokacijama u državi Тексас.

Gradovi u državi Тексас

Zvanični tekst studije (na engleskom)

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Dell Children's Medical Center of Central Texas, Austin
  • Texas Children's Hospital, Houston
Тражи се учесник
Узраст 3 и старији · Оба пола · Ажурирано 9. 11. 2026. · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Neurology Rare Disease Center, Flower Mound
Тражи се учесникФаза 3
0 Days – 42 Days · Оба пола · Ажурирано 23. 10. 2026. · NCT07221669

A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec

  • Neurology Rare Disease Center, Flower Mound
Тражи се учесникФаза 3
0 Days – 7 Months · Оба пола · Ажурирано 15. 10. 2026. · NCT07444450

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Neurology Rare Disease Center, Flower Mound
  • Texas Children's Hospital, Houston
Тражи се учесникФаза 2
Узраст од 5 до 17 · Оба пола · Ажурирано 8. 10. 2026. · NCT07287982

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • University of Texas Southwestern Medical Center, Dallas
  • Neurology Rare Disease Center, Flower Mound
  • Cook Children's Medical Center, Fort Worth
  • и још 1
Тражи се учесникФаза 2
До 2 година · Оба пола · Ажурирано 2. 10. 2026. · NCT07047144

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Texas Childrens Hospital Houston, Houston
Тражи се учесникФаза 1
Узраст 3 и старији · Оба пола · Ажурирано 3. 9. 2026. · NCT06555419

Clinical Procedures to Support Research in ALS

  • University of Texas San Antonio Health Science Center, San Antonio
Тражи се учесникОпсервациона студија
Узраст 18 и старији · Оба пола · Ажурирано 15. 6. 2026. · NCT03489278

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Cook Children's, Fort Worth
  • Texas Children's Hospital, Houston
  • CHRISTUS Health, San Antonio
Тражи се учесникОпсервациона студија
Сви узрасти · Оба пола · Ажурирано 31. 1. 2025. · NCT04174157

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.