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Kliničke studije za Spinalna mišićna atrofija u gradu Norfolk, VA

6 studija za Spinalna mišićna atrofija traži učesnike na lokacijama u gradu Norfolk i okolini (u krugu od oko 30 milja). Otvorite studiju da biste videli ko može da učestvuje i kako kontaktirati tim studije.

Zvanični tekst studije (na engleskom)

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A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

Тражи се учесникФаза 3
  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Узраст од 15 до 60 · Оба пола · Ажурирано 13. 11. 2026. · NCT07444476

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Тражи се учесник
  • Childrens Hospital of the King's Daughters, Norfolk
Узраст 3 и старији · Оба пола · Ажурирано 9. 11. 2026. · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

Тражи се учесникФаза 3
  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
0 Days – 42 Days · Оба пола · Ажурирано 23. 10. 2026. · NCT07221669

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Тражи се учесникФаза 2
  • Childrens Hospital of The Kings Daughters, Norfolk
Узраст од 5 до 17 · Оба пола · Ажурирано 8. 10. 2026. · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Тражи се учесникФаза 1
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
Узраст 3 и старији · Оба пола · Ажурирано 3. 9. 2026. · NCT06555419

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

Тражи се учесникОпсервациона студија
  • Children's Hospital of The King's Daughters, Norfolk
Сви узрасти · Оба пола · Ажурирано 31. 1. 2025. · NCT04174157

Studije za Spinalna mišićna atrofija u drugim gradovima

Ostale studije u gradu Norfolk

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.