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Kliniska studier för Genetiska sjukdomar i Philadelphia, PA
9 studier för Genetiska sjukdomar söker deltagare vid platser i och runt Philadelphia (inom ca 30 miles). Öppna en studie för att se vem som kan delta och hur du kontaktar studieteamet.
Officiell studietext (engelska)
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Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
RekryterarObservationsstudieFriska volontärer välkomna
- University of Pennsylvania, Philadelphia
- Children's Hospital of Philadelphia, Philadelphia
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
RekryterarFas 2/3
- Children's Hospital of Philadelphia, Philadelphia
- Nemours Children's Health, Wilmington · 25 mi bort
Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
RekryterarObservationsstudieFriska volontärer välkomna
- Children's Hospital of Philadelphia, Philadelphia
Rett Syndrome Registry
RekryterarObservationsstudie
- Children's Hospital of Philadelphia, Philadelphia
Rifampin in CYP24A1-related Hypercalcemia and Hypercalciuria
RekryterarFas 2
- Children's Hospital of Philadelphia, Philadelphia
ARPKD Database Study
RekryterarObservationsstudie
- Children's Hospital of Philadelphia, Philadelphia
A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
RekryterarFas 1/2
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
RekryterarFas 1/2
- Children's Hospital of Philadelphia (CHOP), Philadelphia
STXBP1 and SYNGAP1 Related Disorders Natural History Study
RekryterarObservationsstudie
- The Children's Hospital of Philadelphia, Philadelphia
Genetiska sjukdomar-studier i andra städer
- Washington, DC12 studier
- Houston, TX8 studier
- Durham, NC7 studier
- Mountain View, CA6 studier
- Los Angeles, CA6 studier
- Boston, MA6 studier
- Miami, FL5 studier
- New York City, NY5 studier
- San Diego, CA5 studier
- Dallas, TX4 studier
- Chicago, IL4 studier
- Aurora, CO4 studier
Andra studier i Philadelphia
- Cancer (alla typer)59 studier
- Bröstcancer56 studier
- Icke-småcellig lungcancer51 studier
- Metastaserande cancer46 studier
- Prostatacancer44 studier
- Kolorektal cancer44 studier
- Äggstockscancer44 studier
- Lungcancer36 studier
- Akut myeloid leukemi34 studier
- Hjärtsvikt31 studier
- Endometriecancer28 studier
- Depression26 studier
Från ClinicalTrials.gov, data hämtad 6 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.