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Kliniska studier för Leukoencefalopati i Pennsylvania

4 studier för Leukoencefalopati söker deltagare vid platser i Pennsylvania.

Städer i Pennsylvania

Officiell studietext (engelska)

An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

  • Children's Hospital of Philadelphia, Philadelphia
RekryterarFas 1/2
6 Months · Alla kön · Uppdaterad 24 sep. 2026 · NCT05757141

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 9 feb. 2026 · NCT03333200

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • The Children's Hospital of Philadelphia, Philadelphia
  • Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudieFriska volontärer välkomna
Alla åldrar · Alla kön · Uppdaterad 4 feb. 2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 23 okt. 2025 · NCT03047369

Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.