Hem › Leukoencefalopati › Pennsylvania
Kliniska studier för Leukoencefalopati i Pennsylvania
4 studier för Leukoencefalopati söker deltagare vid platser i Pennsylvania.
Städer i Pennsylvania
Officiell studietext (engelska)
An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease
- Children's Hospital of Philadelphia, Philadelphia
RekryterarFas 1/2
6 Months · Alla kön · Uppdaterad 24 sep. 2026 · NCT05757141Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 9 feb. 2026 · NCT03333200North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- The Children's Hospital of Philadelphia, Philadelphia
- Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudieFriska volontärer välkomna
Alla åldrar · Alla kön · Uppdaterad 4 feb. 2026 · NCT01694940The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 23 okt. 2025 · NCT03047369Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.