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Kliniska studier för Spinal muskelatrofi i Kalifornien
11 studier för Spinal muskelatrofi söker deltagare vid platser i Kalifornien.
Städer i Kalifornien
Officiell studietext (engelska)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Stanford University Medical Center, Palo Alto
RekryterarFas 3
Ålder 15 till 60 · Alla kön · Uppdaterad 2 okt. 2026 · NCT07444476A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Hospital of Orange County (CHOC), Orange
- Stanford Neuroscience Health Center (SNHC), Palo Alto
RekryterarFas 2
Upp till ålder 2 · Alla kön · Uppdaterad 2 okt. 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Stanford University Medical Center, Stanford
RekryterarFas 2
Ålder 5 till 17 · Alla kön · Uppdaterad 14 sep. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Valley Children's Hospital, Madera
- Stanford Univ Medical Center, Palo Alto
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 10 sep. 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Children's Hospital of Orange County, Orange
- Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
RekryterarFas 1
Ålder 3 och äldre · Alla kön · Uppdaterad 3 sep. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Children's Hospital Orange County, Orange
- Stanford Medical Center, Palo Alto
- Rady Children's Hospital, San Diego
Rekryterar
Ålder 3 och äldre · Alla kön · Uppdaterad 19 aug. 2026 · NCT05866419Clinical Procedures to Support Research in ALS
- University of California, Irvine, Irvine
- Stanford University, Palo Alto
- California Pacific Medical Center, San Francisco
RekryterarObservationsstudie
Ålder 18 och äldre · Alla kön · Uppdaterad 15 juni 2026 · NCT03489278ALS/MND Natural History Study Data Repository
- Loma Linda University Health, Loma Linda
- Kaiser Permanente, Los Angeles
RekryterarObservationsstudie
Ålder 18 till 90 · Alla kön · Uppdaterad 20 maj 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
RekryterarObservationsstudieFriska volontärer välkomna
Ålder 5 och äldre · Alla kön · Uppdaterad 9 apr. 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Stanford Neuroscience Health Center, Palo Alto
RekryterarObservationsstudie
Ålder 18 till 54 · Kvinnor · Uppdaterad 9 mars 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Children's Hospital of Los Angeles, Los Angeles
- University of California Los Angeles Health, Los Angeles
- Valley Children's Healthcare, Madera
- och 3 fler
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157Från ClinicalTrials.gov, data hämtad 6 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.