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Kliniska studier för Spinal muskelatrofi i Kalifornien

11 studier för Spinal muskelatrofi söker deltagare vid platser i Kalifornien.

Städer i Kalifornien

Officiell studietext (engelska)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
RekryterarFas 2
Upp till ålder 2 · Alla kön · Uppdaterad 2 okt. 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Valley Children's Hospital, Madera
  • Stanford Univ Medical Center, Palo Alto
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 10 sep. 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
RekryterarFas 1
Ålder 3 och äldre · Alla kön · Uppdaterad 3 sep. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Rekryterar
Ålder 3 och äldre · Alla kön · Uppdaterad 19 aug. 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
RekryterarObservationsstudie
Ålder 18 och äldre · Alla kön · Uppdaterad 15 juni 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
RekryterarObservationsstudie
Ålder 18 till 90 · Alla kön · Uppdaterad 20 maj 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
RekryterarObservationsstudieFriska volontärer välkomna
Ålder 5 och äldre · Alla kön · Uppdaterad 9 apr. 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
RekryterarObservationsstudie
Ålder 18 till 54 · Kvinnor · Uppdaterad 9 mars 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • och 3 fler
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157

Från ClinicalTrials.gov, data hämtad 6 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.