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Majaribio ya kliniki ya Magonjwa ya Kurithi katika jimbo la California
Masomo 16 ya Magonjwa ya Kurithi yanatafuta washiriki katika vituo vya jimbo la California.
Miji katika jimbo la California
Maandishi rasmi ya utafiti (Kiingereza)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of California, Los Angeles, Los Angeles
- University of California, Irvine Medical Center, Orange
- Stanford University, Stanford
- na zaidi ya 2
InaajiriUtafiti wa uchunguziWajitolea wenye afya wanakaribishwa
1 Month – 100 Years · Jinsia zote · Imesasishwa 2 Okt 2026 · NCT02450851Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
- UCSF Benioff Children's Hospital Oakland, Oakland
InaajiriHatua 2/3
Umri 2 hadi 17 · Jinsia zote · Imesasishwa 24 Sep 2026 · NCT07441876A Long-Term Observational Study of Patients With Fucosidosis
- Children's Hospital of Orange County, Orange
InaajiriUtafiti wa uchunguzi
Umri wote · Jinsia zote · Imesasishwa 17 Sep 2026 · NCT07615400Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- UCLA Ataxia Center, Los Angeles
InaajiriUtafiti wa uchunguziWajitolea wenye afya wanakaribishwa
Umri wote · Jinsia zote · Imesasishwa 1 Sep 2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 100, Los Angelas
InaajiriHatua 3
Umri 18 hadi 80 · Jinsia zote · Imesasishwa 11 Ago 2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- University of California Irvine, Orange
InaajiriHatua 2
Umri 18 na zaidi · Jinsia zote · Imesasishwa 5 Ago 2026 · NCT07224360Prospective Clinical Assessment Study in Children With Hypochondroplasia
- UCSF Benioff Children's Hospital, Oakland
InaajiriUtafiti wa uchunguzi
30 Months – 16 Years · Jinsia zote · Imesasishwa 16 Jul 2026 · NCT06410976Rett Syndrome Registry
- Children's Hospital Los Angeles, Los Angeles
- UCSF Benioff Children's Hospital, Oakland
- Rady Children's Hospital - San Diego, San Diego
InaajiriUtafiti wa uchunguzi
Umri 0 hadi 99 · Jinsia zote · Imesasishwa 30 Jun 2026 · NCT05432349A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Ronald Reagan UCLA Medical Center, Los Angeles
- University of Stanford Medical Center, Palo Alto
InaajiriHatua 1/2
Umri 1 na zaidi · Jinsia zote · Imesasishwa 23 Mac 2026 · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
- Ronald Reagan UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital Stanford, Stanford
InaajiriHatua 1/2
Umri wote · Jinsia zote · Imesasishwa 22 Jan 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
- UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital at Stanford, Palo Alto
- Altman Clinical and Translational Research Institution, San Diego
InaajiriHatua 1/2
Umri 1 na zaidi · Jinsia zote · Imesasishwa 23 Des 2025 · NCT05295433STXBP1 and SYNGAP1 Related Disorders Natural History Study
- Stanford Medicine Children's Health, Palo Alto
InaajiriUtafiti wa uchunguzi
Umri wote · Jinsia zote · Imesasishwa 29 Okt 2025 · NCT06555965Large Language Models To Improve the Quality of Care of Cardiology Patients
- Stanford, Palo Alto
Inaajiri
Umri 18 na zaidi · Jinsia zote · Imesasishwa 15 Mei 2025 · NCT06935253Natural History Study of Patients with HPDL Mutations
- Eun Hae Lee, San Diego
InaajiriUtafiti wa uchunguzi
Umri wote · Jinsia zote · Imesasishwa 30 Mac 2025 · NCT05848271An Adaptive Clinical Trial of BeginNGS Newborn Screening for Hundreds of Genetic Diseases by Genome Sequencing
- Rady Children's Hospital San Diego, San Diego
InaajiriWajitolea wenye afya wanakaribishwa
1 Day – 28 Days · Jinsia zote · Imesasishwa 12 Mac 2024 · NCT06306521Rady Children's Institute Genomic Biorepository
- Rady Pediatric Genomics & Systems Medicine Institute, San Diego
InaajiriWajitolea wenye afya wanakaribishwa
Umri wote · Jinsia zote · Imesasishwa 12 Des 2022 · NCT02917460Kutoka ClinicalTrials.gov, data iliyopatikana 5 Okt 2026. Kila utafiti una masharti yake ya kufaa; timu ya utafiti huamua nani anaweza kujiunga.