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Glycogen Storage Disease Type II clinical trials in California
5 studies for Glycogen Storage Disease Type II are looking for participants at sites in California.
Cities in California
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
- University of California-Irvine, Irvine
RecruitingPhase 1
Ages 18 to 75 · All sexes · Updated Aug 17, 2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- University of California, Irvine (UCI), Irvine
- Stanford Neuroscience Health Center, Palo Alto
RecruitingPhase 1/2
Ages 18 to 65 · All sexes · Updated Jul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
- University of California at Irvine- Site Number : 840036, Irvine
- Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
- Children's Hospital of Orange County- Site Number : 840074, Orange
- and 3 more
RecruitingObservational study
All ages · All sexes · Updated Jun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of California - Irvine Medical Center, Irvine
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Jun 23, 2026 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of California Irvine, Irvine
RecruitingObservational study
All ages · All sexes · Updated Mar 10, 2026 · NCT06121011From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.