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Spinal Muscular Atrophy clinical trials in Massachusetts
6 studies for Spinal Muscular Atrophy are looking for participants at sites in Massachusetts.
Cities in Massachusetts
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
RecruitingPhase 2
Ages 5 to 17 · All sexes · Updated Sep 14, 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
RecruitingPhase 1
Ages 3 and older · All sexes · Updated Sep 3, 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Recruiting
Ages 3 and older · All sexes · Updated Aug 19, 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
RecruitingObservational study
Ages 18 to 90 · All sexes · Updated May 20, 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
RecruitingObservational studyHealthy volunteers welcome
Ages 5 and older · All sexes · Updated Apr 9, 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
RecruitingObservational study
Ages 18 to 54 · Women · Updated Mar 9, 2026 · NCT05789758From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.