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Gaucher Disease clinical trials in Pittsburgh, PA
5 studies for Gaucher Disease are looking for participants at sites in and around Pittsburgh (within about 30 miles). Open a study to see who can join and how to contact the study team.
Recruiting for a study here? Feature it at the top of this page — $99 for 30 days →
A Gaucher Disease Gene Therapy Trial With FLT201
RecruitingPhase 3
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
RecruitingObservational study
- UPMC Children's Hospital of Pittsburgh- Site Number : 840023, Pittsburgh
Longitudinal Study of Neurodegenerative Disorders
RecruitingObservational study
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
RecruitingObservational study
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
RecruitingPhase 2
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
About Gaucher Disease
Gaucher disease is a rare, inherited disorder in which you do not have enough of an enzyme called glucocerebrosidase. Learn about the three types.
More about Gaucher Disease on MedlinePlus
Gaucher Disease trials in other cities
Other studies in Pittsburgh
- Non-Small Cell Lung Cancer48 studies
- Cancer (all types)41 studies
- Breast Cancer39 studies
- Colorectal Cancer32 studies
- Metastatic Cancer31 studies
- Melanoma31 studies
- Ovarian Cancer30 studies
- Endometrial Cancer23 studies
- Lung Cancer23 studies
- Prostate Cancer23 studies
- Stroke22 studies
- Head and Neck Squamous Cell Carcinoma22 studies
From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.