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Rare Diseases clinical trials in Ohio
8 studies for Rare Diseases are looking for participants at sites in Ohio.
Cities in Ohio
A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Ohio State University, Columbus
RecruitingPhase 1
Ages 18 to 40 · All sexes · Updated Sep 29, 2026 · NCT07180355Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Ohio State University - Neurology, Columbus
RecruitingObservational studyHealthy volunteers welcome
All ages · All sexes · Updated Sep 1, 2026 · NCT06016946International Rare Brain Tumor Registry
- Akron Children's Hospital, Akron
- Cincinnati Children's Hospital Medical Center, Cincinnati
RecruitingObservational study
Up to age 45 · All sexes · Updated Aug 7, 2026 · NCT05697874Evaluation of an Advanced Lower Extremity Neuroprostheses
- Louis Stokes Cleveland VA Medical Center, Cleveland
- MetroHealth System, Cleveland
Recruiting
Ages 21 to 75 · All sexes · Updated Jul 10, 2026 · NCT00623389Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Cincinnati Children's Hospital Medical Center, Cincinnati
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Jun 23, 2026 · NCT07123155A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- University of Cincinnati/Cincinnati Children's Hospital, Cincinnati
- Ohio State University, Columbus
RecruitingPhase 1/2
Ages 25 to 65 · All sexes · Updated May 5, 2026 · NCT06826612The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- University of Cincinnati, Cincinnati
- Ohio State University, Columbus
RecruitingPhase 2
Ages 12 and older · All sexes · Updated Jul 1, 2025 · NCT04372615Epilepsy Learning Healthcare System (ELHS)
- Akron Children's Hospital, Akron
- Cincinnati Children's Hospital Comprehensive Epilepsy Center (CCHMC), Cincinnati
- University of Cincinnati Gardner Neuroscience Institute Epilepsy Center, Cincinnati
RecruitingObservational study
All ages · All sexes · Updated Aug 30, 2024 · NCT06265103From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.