🔎 Trials Near Me

Home › Rare Diseases › Ohio › Cincinnati

Rare Diseases clinical trials in Cincinnati, OH

5 studies for Rare Diseases are looking for participants at sites in and around Cincinnati (within about 30 miles). Open a study to see who can join and how to contact the study team.

International Rare Brain Tumor Registry

RecruitingObservational study
  • Cincinnati Children's Hospital Medical Center, Cincinnati
Up to age 45 · All sexes · Updated Aug 7, 2026 · NCT05697874

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

RecruitingPhase 2
  • Cincinnati Children's Hospital Medical Center, Cincinnati
Ages 18 and older · All sexes · Updated Jun 23, 2026 · NCT07123155

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

RecruitingPhase 1/2
  • University of Cincinnati/Cincinnati Children's Hospital, Cincinnati
Ages 25 to 65 · All sexes · Updated May 5, 2026 · NCT06826612

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

RecruitingPhase 2
  • University of Cincinnati, Cincinnati
Ages 12 and older · All sexes · Updated Jul 1, 2025 · NCT04372615

Epilepsy Learning Healthcare System (ELHS)

RecruitingObservational study
  • Cincinnati Children's Hospital Comprehensive Epilepsy Center (CCHMC), Cincinnati
  • University of Cincinnati Gardner Neuroscience Institute Epilepsy Center, Cincinnati
All ages · All sexes · Updated Aug 30, 2024 · NCT06265103

About Rare Diseases

A rare disease is one that affects fewer than 200,000 people in the United States. There are nearly 7,000, affecting more than 25 million Americans.

More about Rare Diseases on MedlinePlus

Rare Diseases trials in other cities

Other studies in Cincinnati

From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.