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Rare Diseases clinical trials in Cincinnati, OH
5 studies for Rare Diseases are looking for participants at sites in and around Cincinnati (within about 30 miles). Open a study to see who can join and how to contact the study team.
International Rare Brain Tumor Registry
RecruitingObservational study
- Cincinnati Children's Hospital Medical Center, Cincinnati
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
RecruitingPhase 2
- Cincinnati Children's Hospital Medical Center, Cincinnati
A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
RecruitingPhase 1/2
- University of Cincinnati/Cincinnati Children's Hospital, Cincinnati
The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
RecruitingPhase 2
- University of Cincinnati, Cincinnati
Epilepsy Learning Healthcare System (ELHS)
RecruitingObservational study
- Cincinnati Children's Hospital Comprehensive Epilepsy Center (CCHMC), Cincinnati
- University of Cincinnati Gardner Neuroscience Institute Epilepsy Center, Cincinnati
About Rare Diseases
A rare disease is one that affects fewer than 200,000 people in the United States. There are nearly 7,000, affecting more than 25 million Americans.
More about Rare Diseases on MedlinePlus
Rare Diseases trials in other cities
- Boston, MA9 studies
- Washington, DC8 studies
- Chicago, IL8 studies
- Philadelphia, PA7 studies
- Los Angeles, CA5 studies
- Columbus, OH4 studies
- Atlanta, GA3 studies
- St. Louis, MO3 studies
- Seattle, WA3 studies
- Rochester, MN3 studies
- Houston, TX3 studies
- Pittsburgh, PA3 studies
Other studies in Cincinnati
- Non-Small Cell Lung Cancer35 studies
- Cancer (all types)28 studies
- Breast Cancer25 studies
- Heart Failure24 studies
- Colorectal Cancer21 studies
- Acute Myeloid Leukemia20 studies
- Metastatic Cancer20 studies
- Lung Cancer19 studies
- Obesity19 studies
- Ovarian Cancer19 studies
- Prostate Cancer18 studies
- Melanoma17 studies
From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.